Your Voice. Their Blueprint. Hosting an externally-led PFDD (El-PFDD) meeting for Alexander Disease.

Patient-Focused Drug Development (PFDD) means a powerful way for families, caregivers, and people living with a disease to directly tell regulatory decision-makers and treatment developers what living with that condition is really like.

PFDD is a systematic approach to help ensure that patients’ experiences, perspectives, needs, and priorities are captured and meaningfully incorporated into drug development and evaluation.

This is your chance to shape future treatment options with your voice.

Find out more here or download our info sheet.

Please join us and get involved.